Track: WFH
Donna Coffin, MSc
Director, Research & Education
World Federation of Hemophilia
Montreal, Canada
Barbara Konkle, MD (she/her/hers)
Professor of Medicine
Washington Center for Bleeding Disorders
University of Washington
Seattle, United States
Flora Peyvandi, MD, PhD (she/her/hers)
President
ISTH
Milan, Italy
Samantha Gouw, MD PhD
Pediatric Hematologist
Amsterdam UMC
Amsterdam, Netherlands
Cedric Hermans, MD, PhD (he/him/his)
Head, Hemophilia Center
Cliniques Universitaires Saint-Luc
Brussels, Belgium
Barbara Konkle, MD (she/her/hers)
Professor of Medicine
Washington Center for Bleeding Disorders
University of Washington
Seattle, United States
Andrea Laslop, MD (she/her/hers)
Head of Scientific Office
Austrian Medicines and Medical Devices Agency
Vienna, Austria
Vanessa Newman, MD PhD MMed
Medical Consultant GTR
WFH
Witheridge, United Kingdom
Brian O'Mahony, FACSLM
CEO
Irish Haemophilia Society
Dublin, Ireland
Flora Peyvandi, MD, PhD (she/her/hers)
President
ISTH
Milan, Italy
This session will present the WFH Gene Therapy Registry, designed to gather comprehensive data on all people with hemophilia (PWH) who receive gene therapy worldwide. An update on the program, including the governance framework and data governance, will be shared. Additionally, the session will feature insights from various stakeholders, including participating hemophilia treatment centers, national registries, patients, regulatory bodies, and industry.
Chair: Donna Coffin, MSc – World Federation of Hemophilia
Speaker: Barbara Konkle, MD (she/her/hers) – University of Washington
Speaker: Flora Peyvandi, MD, PhD (she/her/hers) – ISTH
Moderator: Barbara Konkle, MD (she/her/hers) – University of Washington
Moderator: Flora Peyvandi, MD, PhD (she/her/hers) – ISTH
Speaker: Cedric Hermans, MD, PhD (he/him/his) – Cliniques Universitaires Saint-Luc
Speaker: Vanessa Newman, MD PhD MMed – WFH
Speaker: Andrea Laslop, MD (she/her/hers) – Austrian Medicines and Medical Devices Agency
Speaker: Samantha Gouw, MD PhD – Amsterdam UMC
Speaker: Brian O'Mahony, FACSLM – Irish Haemophilia Society